1. Giving our Sons with Duchenne the Best Care Possible

    Posted on March 18, 20163:16 pm

        When our son, Hawken, was diagnosed 13 years ago, we were told to go home and love your son…there is nothing you can do.  Those doctors were wrong, there was a lot to be done. Our family was blessed from the beginning to have Jennifer Wallace, PT, come into our lives from day Read more »

  2. Why PTC Withdraws Regulatory Filing in Canada

    Posted on March 14, 20163:39 pm

      PTC withdraws the regulatory filing in Canada so they can supplement the phase II data with the phase III, ACT-DMD data. Why is PTC withdrawing the NDS from Canada? PTC is having ongoing discussions with Health Canada (the equivalent of the FDA in Canada) during the review of their NDS (the equivalent of the Read more »

  3. PTC Therapeutics Patient/Parent Call

    Posted on March 2, 201612:08 am

      Stu Peltz from PTC Therapeutics hosted a call today regarding the Refuse to File letter from the FDA, dated February 22nd.  More detailed information is available in the transcript from the earnings call on February 29. Stu explained the two concerns raised by the FDA: 1)      There was not evidence that this drug would Read more »