1. We need your help to advance a treatment to clinical trials for rare, Duplication 2 mutations!

    Posted on December 15, 20166:56 pm

      CureDuchenne has always been focused on finding and funding treatments to help EVERYONE affected with Duchenne, and to TREAT THE WHOLE DISEASE.  We are very proud of our comprehensive portfolio of research projects and we continue to be the research leader for the Duchenne community. Over the past five years we have pioneered duplication Read more »

  2. Pfizer Clinical Trial Update

    Posted on December 8, 20164:33 pm

      CureDuchenne is pleased to share the following updates from Pfizer pertaining to the on-going multicenter Phase II clinical trial of the investigational compound, domagrozumab (PF-06252616) in boys with Duchenne muscular dystrophy (DMD). Domagrozumab is an experimental, infused, anti-myostatin monoclonal antibody.  Myostatin is a naturally occurring protein in muscles that helps control muscle growth; it Read more »

  3. Bonding Through Stretches

    Posted on December 7, 20165:26 pm

      Guest blog by Paul Miller Our son Hawken was diagnosed with Duchenne in the fall of 2002.  Debra and I rolled up our sleeves and began a journey we had not anticipated.   We found there were many variables to managing this disease.  One of these is physical therapy.  Maintaining the health of the muscles Read more »

  4. Take Action for all Those with Duchenne

    Posted on December 5, 20164:45 pm

      As a community, we need to continue our efforts to find a cure for every single person impacted by Duchenne. That means funding research that treats all aspects of the disease.  That includes anti-inflammatory and anti-fibrosis therapies, gene therapy and gene editing; and cardiac therapies that address the leading cause of death for Duchenne.  Read more »

  5. 21st Century Cures Act Passed by House

    Posted on December 1, 201611:03 pm

      Yesterday the House of Representatives passed the draft of the 21st Century Cures Act. It is slated for a vote in the Senate early next week.       The new draft includes: $4.8 billion in new funding for the National Institutes of Health (NIH) $500 million in new funding for the Food and Read more »