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Dr. Olson Presents on Gene Editing
Today, Dr. Eric Olson, PhD, Chair of Molecular Biology at UT Southwestern, was honored to give a presentation at the American Society of Gene & Cell Therapy (ASGCT) 2017 meeting […]
EMFLAZA Launch Plan
Today, PTC Therapeutics hosted a call for the Duchenne community to announce pricing and services for their launch of EMFLAZA, the commercial name for deflazacort. The announced price will be […]
Duchenne Community Letter from PTC Therapeutics
May 8, 2017 Dear Duchenne Families, Today we shared our plans for the launch of EMFLAZA™ (deflazacort), the first FDA-approved corticosteroid for Duchenne muscular dystrophy patients age 5 and […]
HOPE Clinical Trial Provides Hope for Duchenne Families
CureDuchenne is pleased to see the positive preliminary data from Capricor Therapeutics on their HOPE clinical trial in Duchenne muscular dystrophy. CureDuchenne Ventures helped fund this clinical trial to address […]
Duchenne Community Message From PTC Therapeutics on Close of Emflaza Acquisition
April 20, 2017 Dear Duchenne Community, Today we announced that we have completed our acquisition of Emflaza™ (deflazacort), the first FDA-approved, anti-inflammatory therapy for Duchenne Muscular Dystrophy (DMD) patients […]
Anthem Please Provide Access to Approved Duchenne Treatment
(CureDuchenne letter to Anthem dated March 14) CureDuchenne believes that all those with Duchenne that have a treatment option available to them should have access to the drug. Our heart […]
Letter to Duchenne Community from PTC Therapeutics
We are happy to share the following letter to the Duchenne Community from Stu Peltz, CEO PTC Therapeutics. March 24, 2017 Dear Duchenne Community, We were very excited to […]
PTC-Duchenne Advocacy Community Call, March 21, 2017
Here is a summary of today’s call with PTC’s Patient Advocacy and Commercial Teams Thank you PTC for hosting a call for advocacy leaders this morning to introduce the EMFLAZA […]
Physical Therapist Haydee Bustos is a Pillar of Strength in the Duchenne Community
Haydee Bustos has a passion for helping kids, and through her experience as a physical therapist, she discovered an even deeper desire to help kids with Duchenne muscular dystrophy. […]