We are pleased to share that Edgewise Therapeutics is sponsoring a natural history study in Becker muscular dystrophy, to better understand the course of disease and define endpoints to be used in future clinical trials. The observational study will follow 150 individuals, ages 8 and older, over two years at multiple sites in the US and Europe.
More information is available in the press release below.
You can advance the care, treatment and cure for Duchenne muscular dystrophy. Contributions in any amount can truly make a difference and can be credited to a fundraiser or event from the list below.
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