All News

The Phase 3 PolarisDMD Trial Goes Global

With a flurry of recent activity, 17 trial sites are now open for enrollment. We are especially excited to share that our first international sites in Canada and Australia have […]

UT Southwestern Wellstone Symposium

We are excited about the UT Southwestern Wellstone Symposium on March 30!  Don’t forget to RSVP by March 1.  We’ll see you there!  [download id=”13142″ template=”UT Southwestern Wellstone Symposium “]

NS Pharma Community Letter

We are excited that our industry partner, NS Pharma, has applied for accelertated approval for it’s exon 53 skipping therapy, viltolarsen. We applaud the dedication to the Duchenne community by […]