When it comes to Duchenne muscular dystrophy (DMD), Leonardo Feder knows he’s among the lucky ones. A resident of São Paulo, Brazil’s largest city, Feder was diagnosed with Duchenne at […]
We are excited that our industry partner, NS Pharma, has applied for accelertated approval for it’s exon 53 skipping therapy, viltolarsen. We applaud the dedication to the Duchenne community by […]
We’re pleased to share this letter and news from our partner Santhera about their plans for 2019! For more than 10 years, Santhera has been working on treatments for DMD, […]
In November 2016, two San Diego families received the same devastating news about their little boys. Four-year-old Yannick Etienne and 5-year-old Marko Filenko were each diagnosed with Duchenne muscular dystrophy, […]
Healthcare professionals, personal caregivers and family members of those with Duchenne muscular dystrophy gathered to learn about new data and best practices for steroid use in Duchenne at a webinar […]
Like many mothers of boys with muscular dystrophy, Deborah Hall hasn’t had an easy life. Hall, the daughter of a chemical engineer and a stay-at-home mom, was one of six […]
CRISPR-Cas9 has the ability to change everything about our world. Here’s why it’s awesome and why it’s scary. Outrage continues to grow over the news that Chinese scientist He Jiankui […]
CureDuchenne Webinar with Avidity Biosciences, a privately held biotech company pioneering a new class of precision medicines based upon antibody-oligonucleotide conjugates, to brief the Duchenne community about Avidity’s research in […]
DURHAM – Back in 2003, new mother Debra Miller with her husband, Paul, founded CureDuchenne after their only son was diagnosed with Duchenne, a rapidly progressing form of muscular dystrophy. No […]
