Updates from the INSPIRE DUCHENNE clinical trial of SGT-003, SolidBio’s investigational, next-generation AAV microdystrophin gene therapy candidate brings expanded eligibility criteria, additional trial sites in more regions, and upcoming preliminary data. Both the […]
By Debra Miller, Founder and CEO of CureDuchenne I’m honored to share two transformative events that embody both the resilience of the human spirit and the strength of our community: […]
Annual Event Combines 80’s Fun with Fundraising to Help Find a Cure for Duchenne Muscular Dystrophy San Antonio, Texas (October 30, 2024) – The San Antonio community gathered in style […]
Newport Beach, CA – October 25, 2024 – The first-ever Ladies Luncheon, hosted by CureDuchenne at the beautiful Shady Canyon Golf Club, was a resounding success. This garden party-themed event […]
CureDuchenne is pleased to share that PTC Therapeutics has announced that the FDA has accepted for review the New Drug Application (NDA) for Translarna (ataluren) for the treatment of Duchenne […]
Read a message from our founder and CEO The recently released award-winning Netflix documentary “The Remarkable Life of Ibelin,”* highlights the life of Mats Steen, a Norwegian World of Warcraft […]
Dallas, TX – October 22, 2024– The Dallas community came together in an extraordinary show of support at Champions in Dallas on October 3, 2024, raising $100,000 for CureDuchenne, a […]
Watch the video HERE Pfizer recently provided this video updating the results from their Phase 3 micro-dystrophin gene therapy trial, CIFFREO, which were presented on October 12, 2024 at the […]
Ryan and Paige Getzlaf Pass the Torch to Anaheim Ducks All-Star Troy Terry and His Wife Danielle, Ushering in a New Era for the Iconic Event NEWPORT BEACH, Calif., (September […]
