A letter from Jennifer Wallace Valdes, PT to share with your child’s teachers. This document serves to familiarize them with Duchenne, the physical limitations posed, and reasonable accommodations for the school environment.
CureDuchenne Link is a centralized data hub which combines clinical data, biosamples, and patient reported data for individuals with Duchenne and Becker muscular dystrophy, as well as carriers. Information and samples provided by participants are coded and available for use by approved researchers across the world.
This resource presents anxiety and depression in individuals with Duchenne and introduces cognitive-behavioral strategies to mitigate these issues.
Esta presentación se enfoca en manejar los desafíos asociados con un diagnóstico de Duchenne.
Esta sesión de la conferencia brinda información sobre las terapias emergentes más allá de la restauración de la distrofina, así como actualizaciones/anuncios de las empresas en este espacio.
Vice President, Patient Advocacy & External Innovation
Edgewise Therapeutics
Vice President of Clinical Development
Capricor Therapeutics
This resource offers a view of Clinical Trials 101: what they are, how they run, and how to make decisions surrounding participating in a clinical trial.
Join us for this pre-recorded presentation and Q&A discussing to learn about a new FDA-approved treatment for Duchenne muscular dystrophy. During the session, Catalyst Pharmaceuticals will provide an overview of how this novel corticosteroid works and its efficacy in Duchenne. You will also learn about the journey to comprehensive support and access through the well-established Catalyst Pathways patient support program.
Medical Affairs Director
Catalyst Pharmaceuticals
A brief overview of the rationale behind next generation technology, as well as presentations from the companies in this space. Moderated discussion included.
NS Pharma Industry Presentation:
VILTEPSO®(Viltolarsen) Overview
Shannon Lienert, MD
Medical Science Liaison, Medical Affairs
