Enhancing Muscle Delivery of ASOs to treat Duchenne Dyne is excited to present an overview of their FORCETM platform and DMD drug development program to the Duchenne community and then […]
El impacto de Duchenne en la familia TEMAS: Genética Salud y afrontamiento del portador genético Planificación familiar Hablar con familiares / amigos / médicos / profesores Impacto financiero Se le […]
March 15, 2021 CAMBRIDGE, Mass., March 15, 2021 (GLOBE NEWSWIRE) — Solid Biosciences Inc. (Nasdaq: SLDB), a life sciences company focused on advancing meaningful therapies for Duchenne muscular dystrophy (Duchenne), […]
EDO platform demonstrates potentially best-in-class safety and efficacy profile in addressing DMD and DM1 disease phenotypes Advancing rapidly to the clinic with first-in-human studies expected to initiate in early 2022 […]
This presentation by Kimberly Nugent, CGC at Children’s Hospital of San Antonio is part of The Family Unit webinar and covers the following topics: genetic carrier health, carrier testing options […]
This webinar is a roundtable with scientific and medical experts covering recent updates to COVID-19 vaccines and how they relate to the Duchenne community. You’ll be prompted to enter your […]
Pratteln, Switzerland, March 3, 2021 – Santhera Pharmaceuticals (SIX: SANN) announces that the last patient has completed the last visit for the first period of the placebo-controlled pivotal VISION-DMD study with […]
In this webinar, Sarepta Therapeutics discusses their commitment to individuals living with Duchenne and the community. They provide an overview of their RNA Exon-Skipping therapies as well as Sarepta’s patient […]
This webinar covers the following topics: Co-parenting/caregiving, Marriage and Communication Genetic Carrier Health Ask the Expert Session You’ll be prompted to enter your name and email address to view the […]
