************** Join CureDuchenne and Sarepta on March 4 for a webinar discussing the below announcement. CureDuchenne Webinar: Sarepta Therapeutics update on RNA Exon-Skipping program and Patient Support Services In this […]
Dear Duchenne Community, All of us at Italfarmaco would like to thank the families participating in the Phase 3 EPIDYS trial and in the open label extension study of givinostat […]
Meet the leaders at Edgewise Therapeutics and hear their company goals related to treatments for Duchenne muscular dystrophy. You’ll be prompted to enter your name and email address to view […]
Join us as we continue this educational series through a new lens: Quality of Life. This webinar will cover the following topics:Emergency Care | Dr. Stefan Malin, MD, MSNavigating “Re-entry” […]
Learn more about REGENXBIO’s new gene therapy program for the potential treatment of Duchenne. This webinar provides an overview of the company and RGX-202, a novel, advanced micro-dystrophin gene therapy […]
This webinar provides an update from Astellas on their study to assess the safety, tolerability, and preliminary efficacy of ASP0367 (MA-0211) for boys with Duchenne Muscular Dystrophy. You’ll be prompted […]
PTC Therapeutics shared the below letter to the Duchenne community. We are pleased to see the results of the dystrophin study (Study 045) and thankful for PTC’s longtime commitment to […]
CureDuchenne’s webinar, COVID-19 Vaccines: What the Duchenne Community Needs to Know, was an opportunity for the Duchenne community to get reliable information on COVID-19 vaccines. A panel of experts from […]
NEWPORT BEACH, Calif., Jan. 14, 2021 – CureDuchenne, a leading global nonprofit focused on finding and funding a cure for Duchenne muscular dystrophy, announces a new initiative centered on the COVID-19 vaccine rollout […]
