Premier Wine Series Brought Together Most Acclaimed Napa Valley Vintners Under One Roof in Philadelphia to Benefit Global Nonprofit CureDuchenne NEWPORT BEACH Calif., April 27, 2022 – CureDuchenne, a leading […]
Initiation of AFFINITY DUCHENNE™ trial of RGX-202 for the treatment of Duchenne will be delayed. This January, we shared the news that REGENXBIO received clearance from the U.S. FDA and would […]
Pfizer’s Letter to the Duchenne Community We are pleased to share the good news that several regulatory authorities have approved the re-start of our Phase 3 ambulatory trial (CIFFREO) for […]
Today, Solid Biosciences announced a change to its corporate strategy to better align resources with goals to bring SGT-001 and SGT-003 to patients. Key Takeaways: Enrollment in IGNITE DMD, its […]
We are pleased to share that Edgewise Therapeutics is sponsoring a natural history study in Becker muscular dystrophy, to better understand the course of disease and define endpoints to be […]
Registration Now Open for Three-Day National Conference in Orlando, Welcoming Attendees From Across the Globe Newport Beach, Calif. (March 25, 2022) – CureDuchenne, a leading global nonprofit focused on finding […]
The Event Brought the Austin Community Together for a Night of Fun with a Purpose Featuring Gourmet Food, Cocktails, Casino Games and More NEWPORT BEACH, Calif., April 6, 2022 – […]
How You Can Help Researchers Find Treatments UPDATE: This event has been postponed due to a last-minute issue and will need to be rescheduled. Don’t miss this informative webinar on […]
National Center of Neurology and Psychiatry and Nippon Shinyaku announce positive results for a Phase I/II study evaluating the efficacy and safety of their exon 44 skipping drug (NS-089/NCNP-02) Results […]
